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Inherited Immunodeficiency

Showing 1 - 25 of 2,070

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Primary Immune Deficiency Disorders, Metabolic Disease Trial in Saint Petersburg (Haploidentical Hematopoietic Cell

Recruiting
  • Primary Immune Deficiency Disorders
  • Metabolic Disease
  • Haploidentical Hematopoietic Cell Transplantation
  • Saint Petersburg, Florida
    Johns Hopkins All Children's Hospital
Sep 9, 2021

Primary Immune Deficiency Disorder, Immune Deficiency Disease, Bone Marrow Failure Trial in Baltimore (Alemtuzumab, Fludarabine,

Recruiting
  • Primary Immune Deficiency Disorder
  • +2 more
  • Baltimore, Maryland
    Johns Hopkins University
Oct 20, 2022

Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

Recruiting
  • Primary Immunodeficiency (PID)
  • +4 more
  • data collection
  • Pittsburgh, Pennsylvania
    UPMC Children's Hospital of Pittsburgh
Feb 9, 2022

Genetic Basis of Immunodeficiency

Recruiting
  • Severe Combined Immunodeficiency
    • Bethesda, Maryland
      National Institutes of Health Clinical Center
    Jan 21, 2023

    Breadth of Donor Options for People With Inherited Diseases

    Completed
    • Primary T-cell Immunodeficiency Disorders
    • Common Variable Immunodeficiency
      • Bethesda, Maryland
        National Cancer Institute (NCI)
      Feb 20, 2020

      Immunodeficiency Syndrome, Severe Aplastic Anemia, Genetic Disorder Trial in Nashville, Seattle (procedure, drug, other,

      Terminated
      • Immunodeficiency Syndrome
      • +2 more
      • Allogeneic Bone Marrow Transplantation
      • +8 more
      • Nashville, Tennessee
      • +2 more
      Jan 6, 2021

      Fibroblast-Derived Cell Lines From Skin Biopsies of

      Enrolling by invitation
      • Primary Immunodeficiency
      • +2 more
        • Bethesda, Maryland
          National Institutes of Health Clinical Center
        Jan 18, 2023

        Genetic Diseases of Lymphocyte Homeostasis and Programmed Cell

        Recruiting
        • Primary Immune Deficiency
          • Bethesda, Maryland
          • +6 more
          Feb 2, 2023

          Primary Immunodeficiency Diseases

          Active, not recruiting
          • Wiskott- Aldrich Syndrome
          • ADA Deficient SCID
            • Bethesda, Maryland
              National Institutes of Health Clinical Center
            Jan 13, 2023

            Immunodeficiency Syndrome, Non-Cancer Diagnosis Trial in United States (biological, procedure, drug, other, radiation)

            Completed
            • Immunodeficiency Syndrome
            • Non-Cancer Diagnosis
            • Alemtuzumab
            • +7 more
            • Oakland, California
            • +5 more
            Feb 5, 2020

            Acquired and Inherited Bone Marrow Failure Syndromes

            Recruiting
            • Severe Aplastic Anemia
            • +2 more
              • Bethesda, Maryland
                National Institutes of Health Clinical Center
              Aug 12, 2022

              Evaluation of Patients With Immune Function Abnormalities

              Recruiting
              • Chronic Granulomatous Disease (CGD)
              • +3 more
                • Bethesda, Maryland
                  National Institutes of Health Clinical Center, 9000 Rockville Pi
                Aug 24, 2022

                Neonatal Screening of Severe Combined Immunodeficiencies

                Completed
                • Severe Combined Immunodeficiency
                • Neonatal Screening
                  • Shanghai, Shanghai, China
                    Children's Hospital of Fudan University
                  Jan 3, 2022

                  Allergy and Immunology Natural History Study

                  Recruiting
                  • Immune Deficiency
                  • +2 more
                    • New York, New York
                      Columbia University Irving Medical Center / NewYork-Presbyterian
                    Oct 14, 2022

                    Peripheral Blood Hematopoietic Stem Cells, Mononuclear Cells and

                    Recruiting
                    • Granuloma
                    • +4 more
                      • Bethesda, Maryland
                        National Institutes of Health Clinical Center
                      Jan 25, 2023

                      Immunologic Deficiency Syndromes Trial in Milano (Strimvelis)

                      Enrolling by invitation
                      • Immunologic Deficiency Syndromes
                      • Strimvelis
                      • Milano, Lombardia, Italy
                        Orchard Investigational Site
                      Jun 23, 2021

                      Genetic Analysis of Immune Disorders

                      Recruiting
                      • DOK 8
                      • +4 more
                        • Bethesda, Maryland
                          National Institutes of Health Clinical Center
                        Jan 27, 2023

                        Intestinal Inflammation in People With Primary Immune

                        Recruiting
                        • Chronic Granulomatous Disease
                        • Inflammatory Bowel Disease
                          • Bethesda, Maryland
                            National Institutes of Health Clinical Center
                          Jan 23, 2023

                          GATA2, Immunodeficiency Trial run by the National Cancer Institute (NCI) (drug, radiation, procedure)

                          Not yet recruiting
                          • GATA2
                          • Immunodeficiency
                          • Mycophenolate Mofetil
                          • +7 more
                          • Bethesda, Maryland
                            National Institutes of Health Clinical Center
                          Jun 23, 2023

                          Non-Neoplastic Hematologic and Lymphocytic Disorder Trial in United States (procedure, biological, drug, other, radiation)

                          Completed
                          • Non-Neoplastic Hematologic and Lymphocytic Disorder
                          • Allogeneic Bone Marrow Transplantation
                          • +11 more
                          • Aurora, Colorado
                          • +5 more
                          Jul 21, 2021

                          Primary Immunodeficiencies in Patients Hospitalized for Severe

                          Recruiting
                          • Primary Immunodeficiency
                            • Montpellier, France
                              Uhmontpellier
                            Oct 11, 2021

                            Antithrombin III Deficiency Trial in Brussel (observation)

                            Not yet recruiting
                            • Antithrombin III Deficiency
                            • observation
                            • Brussel, Belgium
                              UZ Brussel
                            May 26, 2023

                            X-linked Severe Combined Immunodeficiency Trial in Paris (Gene transfer)

                            Completed
                            • X-linked Severe Combined Immunodeficiency
                            • Gene transfer
                            • Paris, France
                              Hopital Necker
                            Sep 22, 2021

                            Human Immunodeficiency Virus Infection, Osteoporosis, Osteoporosis Risk Trial (Patient Participation Form)

                            Not yet recruiting
                            • Human Immunodeficiency Virus Infection
                            • +2 more
                            • Patient Participation Form
                            • (no location specified)
                            Mar 3, 2023

                            Exercise Capacity, Physical Activity Level and Quality of Life

                            Recruiting
                            • Primary Immunodeficiency Diseases
                              • Ankara, Çankaya, Turkey
                                Gazi University, Faculty of Health Sciences, Department of Physi
                              Aug 13, 2023